Product Pipeline
Drug Candidate
Indication
Commercial Right
US
Partners
Regulatory Designation
ASC-930
GVHD
Global
- Discovery
- Preclinical
- Phase 1/2a
- Phase 2b
Cell Therapy
Orphan drug designation
ASC-618
Hemophilia A
Global
Gene Therapy
FDA Orphan Drug Designation/Fast Track Designation; EMA Orphan Drug Designation
ASC-518
Hemophilia A
Partnered
Gene Editing
ASC-519
Hemophilia B
Partnered
Gene Editing
ASC-520
β-Thalassemia
Partnered
Gene Editing
abc
Leading Products
Our current pipeline is focused on blood diseases. We are devoted to discovering, developing and delivering cures for intractable diseases using gene and cell therapies.
Not only do we have experienced teams for discovery research, CMC, pre-clinical and clinical development, we also collaborate with leading academic and industry partners around the world to advance and expand our product pipeline. Building upon our deep knowledge in stem cell, gene therapy and genome editing technology, we are devoted to discovering, developing and delivering cures for intractable diseases.
Our Pipeline
Drug Candidate
Indication
Commercial Right
US
Partners
Regulatory Designation
ASC-930
GHVD
Global
- Discovery
- Preclinical
- Phase 1/2a
- Phase 2b
Cell Therapy
Orphan drug designation
ASC-618
Hemophilia A
Global
Gene Therapy
Orphan drug designation
ASC-518
Hemophilia A
Partnered
Gene Editing
ASC-519
Hemophilia B
Partnered
Gene Editing
ASC-520
β-Thalassemia
Partnered
Gene Editing
abc
Leading Products
Our current pipeline is focused on blood diseases. We are devoted to discovering, developing and delivering cures for intractable diseases using gene and cell therapies.
Not only do we have experienced teams for discovery research, CMC, pre-clinical and clinical development, we also collaborate with leading academic and industry partners around the world to advance and expand our product pipeline. Building upon our deep knowledge in stem cell, gene therapy and genome editing technology, we are devoted to discovering, developing and delivering cures for intractable diseases.