MSUD Advisory Board
Guangping Gao, PhD
AAV gene therapy pioneer
Co-Director, Li Weibo Institute for Rare Diseases Research, Director, Horae Gene Therapy Center and Viral Vector Core, Professor of Microbiology and Physiological Systems, Penelope Booth Rockwell Professor in Biomedical Research, University of Massachusetts Medical School
Kevin Strauss, MD
PI of Zolgensma clinical trial
Principal Investigator on a number of industry sponsored and investigator initiated clinical studies to identify disease-modifying therapies for spinal muscular atrophy, phenylketonuria (PKU), Crigler-Najjar syndrome, and more.
Dan Wang, PhD
EXPERT IN AAV GENE THERAPY RESEARCH
Assistant Professor at the University of Massachusetts. The Wang Lab research program is built at the interface between AAV gene delivery, molecular biology, and tool development. Current research focuses on rAAV engineering, in vivo rAAV-mediated gene delivery methods targeting rare diseases, especially MSUD, and assessing immunological barriers in gene therapy.
Guangping Gao, PhD
AAV gene therapy pioneer
Principal Investigator on a number of industry sponsored and investigator initiated clinical studies to identify disease-modifying therapies for spinal muscular atrophy, phenylketonuria (PKU), Crigler-Najjar syndrome, and more.
Kevin Strauss, MD
PI of Zolgensma gene therapy
Principal Investigator on a number of industry sponsored and investigator initiated clinical studies to identify disease-modifying therapies for spinal muscular atrophy, phenylketonuria (PKU), Crigler-Najjar syndrome, and more.
Guangping Gao, PhD
Biomedical Research, University of Massachusetts Medical School
Assistant Professor at the University of Massachusetts. The Wang Lab research program is built at the interface between AAV gene delivery, molecular biology, and tool development. Current research focuses on rAAV engineering, in vivo rAAV-mediated gene delivery methods targeting rare diseases, especially MSUD, and assessing immunological barriers in gene therapy.