Guangping Gao and Dan Wang partner with ASC Therapeutics to develop novel gene therapy for maple syrup urine disease

UMass Medical School researchers Guangping Gao, PhD, and Dan Wang, PhD, are working with ASC Therapeutics, a privately held biopharmaceutical company developing in-vivo gene replacement, gene editing and allogeneic cell therapies, to bring a gene therapy for maple syrup urine disease (MSUD) to the clinic. “Our significant progress developing an AAV-based therapy for MSUD will … Read more

ASC Therapeutics Announces Partnership With University of Massachusetts Medical School to Co-Develop Novel Gene Therapy for Maple Syrup Urine Disease

MILPITAS, Calif.–(BUSINESS WIRE)–ASC Therapeutics, a privately-held biopharmaceutical company pioneering the development of transformative in-vivo gene replacement, gene editing and allogeneic cell therapies, today announced a partnership with the University of Massachusetts Medical School (UMMS) to co-develop a gene therapy for Maple Syrup Urine Disease (MSUD). “We look forward to working with the UMMS team led … Read more

Phase 1/2 Trial Set to Test ASC618, Gene Therapy for Hemophilia A

The U.S. Food and Drug Administration (FDA) has approved ASC Therapeutics’ request to open a clinical trial in the U.S. into the safety and early efficacy of ASC618, its second-generation gene therapy for hemophilia A. A Phase 1/2 trial (NCT04676048), set to start this month, will test the one-time therapy in up to 12 adults with moderate … Read more

ASC Therapeutics Receives IND Clearance From the U.S. Food and Drug Administration for ASC618 Second-Generation Gene Therapy for Hemophilia A

BusinessWire Transformational in-vivo AAV gene therapy for hemophilia A Efficiently biosynthesized and secreted bioengineered factor VIII Potentially leads to lower vector dose, reduced cost and extended durability MILPITAS, Calif.–ASC Therapeutics, a privately-held biopharmaceutical company pioneering the development of transformative in-vivo gene replacement, gene editing and allogeneic cell therapies for hematologic and other rare disorders today … Read more

ASC Therapeutics “Advanced Genome Editing, Gene & Cell Therapy Platforms in the US and China” won the first prize

ASC Therapeutics “Advanced Genome Editing, Gene & Cell Therapy Platforms in the US and China” won the first prize of the “2021 Fifth Forum For New Drug R&D And Bio-Pharma Projects Roadshow” held on June 24, 2021 in Nanjing Biomedical Valley. Our CEO Ruhong Jiang, PhD, described our three platforms for second-generation gene therapy, CRISPR … Read more