Our Technology
We are developing gene and cell-based therapies. Gene therapy is addition, alteration or removal of genes within cells and biological tissues to treat diseases. A correcting genetic agent can be delivered directly to the blood stream in vivo, or to the affected tissue in situ, or the targeted cells can be modified ex vivo and injected back to the patients. Cell-based therapies involve injecting or implanting intact or genetically modified cells to the patients, where the cells themselves act as a curative agent.
For gene editing, we developed improved CRISPR/CAS and TARGATT™ technologies to deliver precision genetic editing or gene replacement.
Gene delivery system is key in gene therapy. Our therapeutics team is working with state-of-the-art systems including recombinant Adeno-Associated Viruses and lipid-nanoparticles.
Gene Therapy
Cell therapy is indicated for human diseases that cannot be treated by other interventions and require the identification, expansion and potentially genetic or pharmacological manipulation of selected cells.
Gene Editing
Gene editing is a type of genetic engineering allowing the addition, removal or alteration of genetic material at particular locations in the genome. Our team has successfully applied our proprietary integrase-driven technology, TARGATT, and CRISPR-CAS9 techniques.
Cell Therapy
Cell therapy is indicated for human diseases that cannot be treated by other interventions and require the identification, expansion and potentially genetic or pharmacological manipulation of selected cells.